OUR SCIENCE GOALS Our immediate goal is to find a treatment for free sialic acid storage disorder (FSASD) within the next 5 years. Our ultimate hope is to fully eradicate Salla disease through the use of groundbreaking gene editing technology. In April and May, the National Institutes of Health will take six Salla children to create an official natural history study. This work is crucial to create the necessary biomarkers to study therapy options and efficacy in patients. 7